Duarte galactosemia

Applied Therapeutics to Present New Data on Prevention and Treatment of Galactosemia Complications at the Galactosemia Foundation Conference

Retrieved on: 
Wednesday, July 11, 2018

The data presentation, entitled "A Novel Investigational Treatment in Preclinical Development for Galactosemia," will be presented on Saturday, July 14 at 3:30 p.m. MT.

Key Points: 
  • The data presentation, entitled "A Novel Investigational Treatment in Preclinical Development for Galactosemia," will be presented on Saturday, July 14 at 3:30 p.m. MT.
  • Oral treatment of neonatal rats once daily with AT-007 effectively prevented complications associated with galactosemia in a model of Classic Galactosemia.
  • Additional data on prevention of complications associated with galactitol formation will be presented.
  • For more information about galactosemia, please visit the Galactosemia Foundation website or the National Organization for Rare Disorders (NORD) website .