NNPDF

Zevra Therapeutics Celebrates and Supports Global Niemann-Pick Disease Awareness Day on October 19th and Niemann-Pick Disease Awareness Month Throughout October

Retrieved on: 
Thursday, October 19, 2023

CELEBRATION, Fla., Oct. 19, 2023 (GLOBE NEWSWIRE) -- Zevra Therapeutics, Inc. (NasdaqGS: ZVRA), a rare disease therapeutics company, proudly supports the Niemann-Pick community on Global Niemann-Pick Disease Awareness Day and throughout Niemann-Pick Disease Awareness Month.

Key Points: 
  • CELEBRATION, Fla., Oct. 19, 2023 (GLOBE NEWSWIRE) -- Zevra Therapeutics, Inc. (NasdaqGS: ZVRA), a rare disease therapeutics company, proudly supports the Niemann-Pick community on Global Niemann-Pick Disease Awareness Day and throughout Niemann-Pick Disease Awareness Month.
  • Patient organizations like the International Niemann-Pick Disease Alliance (INPDA) and the National Niemann-Pick Disease Foundation (NNPDF) provide essential support for people living with Niemann-Pick disease type C (NPC) and their families and advocate for needed treatments.
  • “So many members of the advocacy community around the world work tirelessly to support people who live with NPC and raise awareness of this devastating disease.
  • “It is an ultra-rare, genetic, relentlessly progressive neurodegenerative disease impacting approximately 1 in 100,000 live births.

Zevra Therapeutics to Participate in the 2023 NNPDF Family Support and Medical Conference

Retrieved on: 
Wednesday, July 19, 2023

CELEBRATION, Fla., July 19, 2023 (GLOBE NEWSWIRE) -- Zevra Therapeutics, Inc. (NasdaqGS: ZVRA) (Zevra, or the Company, formerly KemPharm, Inc.), a rare disease therapeutics company, today announced their support of the upcoming National Niemann-Pick Disease Foundation’s (NNPDF) Family Support and Medical Conference.

Key Points: 
  • CELEBRATION, Fla., July 19, 2023 (GLOBE NEWSWIRE) -- Zevra Therapeutics, Inc. (NasdaqGS: ZVRA) (Zevra, or the Company, formerly KemPharm, Inc.), a rare disease therapeutics company, today announced their support of the upcoming National Niemann-Pick Disease Foundation’s (NNPDF) Family Support and Medical Conference.
  • Members of the Zevra team will attend this event which is being held in Orlando, Florida, from July 20 through July 22, 2023.
  • In addition to providing a corporate update, Zevra plans to lead a family working group session to gain insights from caregivers on important topics facing the rare disease community.
  • “The Zevra team is proud to sponsor the NNPDF and their work supporting the patients and their families who continue to inspire us with their strength and hope.

KemPharm Supports Niemann-Pick Awareness Month During October and Global Niemann-Pick Awareness Day on October 19th

Retrieved on: 
Tuesday, October 4, 2022

CELEBRATION, Fla., Oct. 04, 2022 (GLOBE NEWSWIRE) -- KemPharm, Inc.(NasdaqGS: KMPH) (KemPharm, or the Company), a biotechnology company focused on the discovery, development and commercialization of novel treatments for rare diseases, announced its support for Niemann-Pick Awareness Month, which is the month of October, and Global Niemann-Pick Awareness Day, which is October 19th.

Key Points: 
  • CELEBRATION, Fla., Oct. 04, 2022 (GLOBE NEWSWIRE) -- KemPharm, Inc.(NasdaqGS: KMPH) (KemPharm, or the Company), a biotechnology company focused on the discovery, development and commercialization of novel treatments for rare diseases, announced its support for Niemann-Pick Awareness Month, which is the month of October, and Global Niemann-Pick Awareness Day, which is October 19th.
  • KemPharm supports and unites with these groups in advocating for those affected by NPC and their families and in seeking new therapeutic options for NPC where no satisfactory alternative treatments currently exist.
  • KemPharm is a biotechnology company focused on the discovery, development and commercialization of novel treatments for rare diseases.
  • KemPharm has a diverse product portfolio, combining a clinical-stage development pipeline with NDA-stage and commercial assets.

KemPharm to Participate in the 2022 Joint NNPDF-INPDA Conference and Meeting

Retrieved on: 
Tuesday, July 26, 2022

The joint event is being held in Orlando, Florida, from July 28 through August 1, 2022.

Key Points: 
  • The joint event is being held in Orlando, Florida, from July 28 through August 1, 2022.
  • Our presence and sponsorship of these events demonstrate our commitment to both the U.S. and international NPC advocacy community.
  • KemPharm is a specialty pharmaceutical company focused on the discovery, development and commercialization of novel treatments for rare central nervous system (CNS), neurodegenerative and lysosomal storage diseases.
  • KemPharm has a diverse product portfolio, which includes a pipeline of several clinical-stage product candidates that are intended for orphan/rare disease indications.

Cyclo Therapeutics to Present at the NNPDF-INPDA Conferences 2022

Retrieved on: 
Thursday, July 21, 2022

The presentations at the NNPDF-INPDA conferences will be open to registered attendees and the respective conferences, both in person and virtually.

Key Points: 
  • The presentations at the NNPDF-INPDA conferences will be open to registered attendees and the respective conferences, both in person and virtually.
  • Founded in 1993, NNPDF serves families throughout the nation at all stages of their Niemann-Pick journey.
  • Cyclo Therapeutics, Inc. is a clinical-stage biotechnology company dedicated to developing life-changing medicines through science and innovation for patients and families suffering from disease.
  • Statements that are not historical facts, such as anticipates, believes and expects or similar expressions, are forward-looking statements.

Cyclo Therapeutics Recognizes Niemann-Pick Disease Awareness Month Highlighting Need for Broader Awareness and Support for Research to Find a Treatment

Retrieved on: 
Tuesday, October 19, 2021

Symptoms of the disease include enlarged liver or spleen, difficulties with motor skills, speech, swallowing and feeding as well as cognitive impairment.

Key Points: 
  • Symptoms of the disease include enlarged liver or spleen, difficulties with motor skills, speech, swallowing and feeding as well as cognitive impairment.
  • In honor of Niemann-Pick Disease Awareness Month, Cyclo Therapeutics will be engaging in several initiatives to help raise awareness and provide information on research and support for patients and families.
  • The launch of NPCspotlight.com , a new website with information about the disease and perspectives from patients and others about living with NPC.
  • Cyclo Therapeutics, Inc. is a clinical-stage biotechnology company dedicated to developing life-changing medicines through science and innovation for patients and families suffering from disease.

National Niemann-Pick Disease Foundation Honors Global Niemann-Pick Awareness Day Highlighting Need for Broader Support and Research

Retrieved on: 
Tuesday, October 19, 2021

FORT ATKINSON, Wis., Oct. 19, 2021 /PRNewswire/ --The National Niemann-Pick Disease Foundation (NNPDF), the leading advocacy organization for people living with Niemann-Pick disease in the United States, today commemorates the third annual Niemann-Pick Disease Awareness Day, a global effort to build awareness of the significant impact this rare genetic disease has on patients, caregivers and families.

Key Points: 
  • FORT ATKINSON, Wis., Oct. 19, 2021 /PRNewswire/ --The National Niemann-Pick Disease Foundation (NNPDF), the leading advocacy organization for people living with Niemann-Pick disease in the United States, today commemorates the third annual Niemann-Pick Disease Awareness Day, a global effort to build awareness of the significant impact this rare genetic disease has on patients, caregivers and families.
  • NNPDF joins with the global community to honor patients and families and to highlight the critical need for increased awareness and research that can lead to new treatments and services for people affected by the disease.
  • "In the past year, we have faced many challenging setbacks, but our community stayed together to continue fighting and advocating for all those affected by Niemann-Pick disease.
  • The National Niemann-Pick Disease Foundation, Inc. (NNPDF) is a non-profit patient advocacy and family support organization dedicated to supporting and empowering patients and families affected by Niemann-Pick disease through education, collaboration and research.

National Niemann-Pick Disease Foundation Recognizes Annual Global Niemann-Pick Awareness Day

Retrieved on: 
Monday, October 19, 2020

FORT ATKINSON, Wis., Oct. 19, 2020 /PRNewswire/ --The National Niemann-Pick Disease Foundation (NNPDF), the leading advocacy organization for people living with Niemann-Pick disease in the United States, today recognizes international Niemann-Pick Awareness Day, a global initiative to build awareness of the significant impact this rare genetic disease has on patients, caregivers, and families.

Key Points: 
  • FORT ATKINSON, Wis., Oct. 19, 2020 /PRNewswire/ --The National Niemann-Pick Disease Foundation (NNPDF), the leading advocacy organization for people living with Niemann-Pick disease in the United States, today recognizes international Niemann-Pick Awareness Day, a global initiative to build awareness of the significant impact this rare genetic disease has on patients, caregivers, and families.
  • "Global Niemann-Pick Awareness Day has become a strong international platform to raise awareness of this disease that currently has no approved treatments.
  • "Niemann-Pick Awareness Day is also a time to recognize and honor all the families who have joined in the effort to build awareness and support others.
  • The National Niemann-Pick Disease Foundation, Inc. (NNPDF) is a non-profit patient advocacy and family support organization dedicated to supporting and empowering patients and families affected by Niemann-Pick disease, through education, collaboration and research.

CTD Announces New Data Presented at Annual Gathering of Patients and Families Tackling Niemann-Pick Disease Type C

Retrieved on: 
Thursday, August 15, 2019

The companys presentation to families will be made on August 16, followed by a Q & A session.

Key Points: 
  • The companys presentation to families will be made on August 16, followed by a Q & A session.
  • CTD announced its participation at the conference and support for the conference via an unrestricted grant in a release July 31, 2019.
  • Niemann-Pick type C Disease (NPC) is a rare, genetic disease affecting 1 in 100,000 live births globally.
  • The National Niemann-Pick Disease Foundation (NNPDF) is a non-profit organization dedicated to supporting and empowering patients and families affected by Niemann Pick Disease through education, collaboration, and research.

CTD Announces Support and Participation at Annual Family Conference of National Niemann-Pick Disease Foundation

Retrieved on: 
Wednesday, July 31, 2019

The NNPDF is a non-profit organization dedicated to supporting and empowering patients and families affected by Niemann-Pick Disease through education, collaboration and research.

Key Points: 
  • The NNPDF is a non-profit organization dedicated to supporting and empowering patients and families affected by Niemann-Pick Disease through education, collaboration and research.
  • This is CTDs fourth year of supporting the conference with an unrestricted grant and in presenting on the companys clinical program in Niemann-Pick Disease Type C (NPC).
  • Said CTD Chairman and CEO N. Scott Fine, The NNPDF annual gathering represents an important venue for us to learn and share.
  • Added NNPDF Executive Director Joslyn Crowe, Without sponsor support, the annual gatherings of families who are struggling with NPC would not be possible.